This Saturday is the thirty ninth version of Virades de l’Espoir, an occasion which raises funds for the combat in opposition to cystic fibrosis and raises consciousness of this illness among the many normal public. An occasion which takes place as Kaftrio, a revolutionary therapy, is made accessible for kids aged 2 to five years outdated affected by the illness.
Excellent news for 500 youngsters aged 2 to five years outdated affected by Cystic Fibrosis. They may be capable to have early entry to the Kaftrio drug. The Excessive Authority of Well being has issued a optimistic opinion on this revolutionary therapy. In December 2022, this therapy was approved for kids aged 6 to 11.
Extraordinarily favorable outlook
“This authorization is good news,” rejoices David Fiant, president of the Vaincre la Mucoviscidose affiliation, “it can permit sufferers aged 2 to five years to acquire very efficient therapy at an age the place the signs of cystic fibrosis usually happen. Cystic fibrosis usually are not but too marked. This therapy can additional defend their respiratory and digestive techniques.
Research carried out in youngsters aged 6 to 11 have proven a discount within the typical signs of the illness, reminiscent of lung infections which might result in very heavy intravenous antibiotic therapies. “We additionally see the long-term threat of getting irreversible lung injury receding, the ultimate consequence of which is lung transplant, and even worse.” These are due to this fact extraordinarily favorable prospects for a illness which nonetheless stays incurable at the moment.